Stargardt disease is an inherited retinal disorder caused by mutations in the ABCA4 gene. It is the most common form of juvenile macular degeneration, leading to progressive central vision loss ...

The therapy, OCU410ST (AAV-hRORA), represents a novel approach in treating Stargardt disease through a one-time modifier gene therapy aimed at providing lifelong benefits. “The completion of ...

A Potential Game-Changer for Stargardt Disease Stargardt disease, a progressive genetic eye disorder that leads to vision ...

SB-007 addresses the root cause of Stargardt disease with the potential to treat all patients across all ABCA4 mutations SB-007 is the first dual AAV gene therapy in clinical development for ...