SpliceBio, a clinical-stage genetic medicines company, announced that it has dosed the first patient in the phase ½ Astra ...

Stargardt disease happens when fatty material builds up on the macula – the small part of the retina needed for central ...

The Stargardt Disease market is expected to surge due to the disease's increasing prevalence and awareness during the ...

Meanwhile, OCU410ST targets Stargardt disease, a rare genetic condition ... The goal is a one-time treatment designed to preserve vision and improve quality of life for patients with progressive ...

A blind climber who scales 25m (82ft) walls using touch and his brother's spoken directions has raised £14,000 towards his ...

Vutrisiran is already approved as Amvuttra to treat rare disease hereditary ATTR amyloidosis, so approval in Stargardt disease ... area of the retina and affect vision. There is currently no ...

Stargardt disease is an inherited retinal disorder caused by mutations in the ABCA4 gene. It is the most common form of juvenile macular degeneration, leading to progressive central vision loss ...

he was diagnosed with Stargardt disease, a rare and degenerative eye condition. Think of everything shrouded in a haze, or images appearing in spots, or dark holes inside your vision where ...

We target critical pathways underlying retinal diseases using innovative small molecules to slow, stop, or restore vision ...