Kathy Bleitz suffers from a condition called Stargardt disease and has been legally blind since the age of 11. It’s an inherited degenerative disease that significantly reduces vision in the ...

The Stargardt Disease market is expected to surge due to the disease's increasing prevalence and awareness during the ...

Alnylam has said it will not proceed with a clinical trial of its RNAi drug vutrisiran in the rare eye disorder Stargardt disease – at ... of the retina and affect vision. There is currently ...

Stargardt disease is an inherited retinal disorder caused by mutations in the ABCA4 gene. It is the most common form of juvenile macular degeneration, leading to progressive central vision loss ...

and the Pioneer Drug Designation in Japan for Stargardt disease, for which there are no approved treatments. The study design for the DRAGON trial included an adaptive sample size re-estimation that ...