A Lower Hutt family relocates to access Trikafta for their 4-year-old daughter, aiming to prevent further irreversible damage from CF. Video / Herald NOW Young children suffering permanent damage from ...

Keller Central assistant coach Derek Hill, who battles cystic fibrosis daily, with his wife, LaNaya, and their daughter, Emersyn. Hill family Courtesy to the Star-Telegram Derek Hill admits he’s ...

In a mixed interim data drop, Arcturus Therapeutics has revealed a lack of efficacy for its investigational inhaled mRNA therapy in cystic fibrosis (CF). The findings, shared today before market open, ...

Investing.com -- Arcturus Therapeutics Holdings Inc. (NASDAQ:ARCT) stock fell 50% Wednesday after the company released interim Phase 2 data for its cystic fibrosis treatment that failed to show ...

To topple access barriers to Vertex Pharmaceuticals’ potentially lifesaving, yet often out-of-reach cystic fibrosis therapy Trikafta, a buyers club has resurfaced with a plan to introduce a discounted ...

A bereaved mum has opened up on the passing of her unborn daughter to mark baby loss awareness week. Sophie Bloor described the pain as being ‘like nothing else’. The 26-year-old became pregnant with ...

EMERYVILLE, Calif., Oct. 13, 2025 (GLOBE NEWSWIRE) -- 4D Molecular Therapeutics (Nasdaq: FDMT, 4DMT, or the Company), a leading late-stage biotechnology company advancing durable and disease-targeted ...

The European Medicines Agency (EMA) has recommended granting marketing authorization in the EU for brensocatib (Brinsupri, Insmed Incorporated) for non-cystic fibrosis bronchiectasis (NCFB) in ...

After only 28 days of treatment with ARCT-032 (10 mg), 4 out of 6 Class I CF participants exhibited encouraging reduction of mucus plug number and mucus volume 12-week study enrolling up to 20 CF ...

- Data presented on outcomes following treatment with CFTR modulators add to growing body of evidence that reduced level of sweat chloride is associated with improved clinical outcomes, particularly ...