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The university has been awarded a £1m grant from LifeArc and Muscular Dystrophy UK Researchers from University College London (UCL) are aiming to develop potential treatments for congenital muscular ...
Muscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, causing them to weaken and deteriorate over time. While muscular dystrophies are ...
Global Duchenne Muscular Dystrophy Drugs Market value attained USD 3.9 Billion in 2025. The market will achieve USD 6.5 Billion during 2034 with a growth rate (CAGR) of 10.96% during the forecast ...
So it's refreshing to see the resilience of the human spirit. Muscular dystrophy is untreatable as a misconception, and I think that even in those that don't have a targeted genetic therapy ...
A national-level workshop on muscular dystrophy and related genetic disorders was held at the Integrated Muscular Dystrophy Rehabilitation Centre (IMDRC), Manav Mandir, in Kothon village.
SAN DIEGO — Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory boys with Duchenne muscular dystrophy, interim data show.
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain ...
More information: Dariusz C. Górecki et al, Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy (2025). DOI: 10.1038/s41434-025-00531-y ...
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Suneel Ram’s needs gradually became greater after he was diagnosed at age 3 with Duchenne muscular dystrophy, a muscle-wasting genetic disorder that afflicts one in 5,000 boys. Today ...
Children with a rare form of muscular dystrophy have been promised access to a groundbreaking drug after the Sunday Mail highlighted their plight. Around 30 boys could have their lives extended by ...