The U.S. Food and Drug Administration said on Friday it approved new labeling for Sarepta Therapeutics' gene therapy Elevidys ...

There's a new frontier in treating autoimmune diseases. Today's treatments tamp down the friendly fire but don't fix what's ...

GLP-1s are being studied for a wide range of conditions. Now, scientists will test whether their anti-inflammatory properties ...

Sarepta Therapeutics Inc.’s controversial gene therapy for a rare muscle condition will remain available in the US with a ...

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.

A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients.

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year ...

Promising results from a small clinical trial highlight a growing interest in designing gene-editing treatments for common ...

The updated label now includes a boxed warning and a new “limitation of use" in addition to the removal of the prior ...

The drug enlicitide reduced cholesterol for adults with high levels due to an inherited disorder and may also work for a broader population.

Rilparencel, a percutaneous minimally invasive injectable product prepared from patients’ own kidney cells, is being developed to treat those with stage 3b or 4 CKD and either type 1 or type 2 ...