Cross-species BBB-penetrant IV-delivered AAV gene therapy provides broad and robust CNS tau lowering in tauopathy mouse models and non-human primate (#559). Hechen Bao, Ph.D., Scientist II, ...

Aug. 7, 2024 — Bioengineers have developed a noninvasive tool to measure gene expression and gene therapy delivery in specific brain regions using ... New Gene Therapy Approach Shows Promise for ...

The yeast RGG motif-containing RNA binding protein Scd6 and its human ortholog LSM14A regulate the translation of specific ...

Most cells in the human body each contain about six feet of DNA. Yet the nucleus, where DNA is coiled, is no larger than a ...

Zevra Therapeutics, Inc. (NasdaqGS: ZVRA) (Zevra, or the Company), a commercial-stage company focused on providing therapies for people living with rare disease, today announces the publication of ...

Single cell techniques have revolutionized molecular life sciences. Ari Pekka Mähönen’s research group used single cell RNA sequencing to generate high resolution gene expression map of Arabidopsis ...

CGT Catapult is an independent technology and innovation organization specializing in the advancement of the cell and gene therapy industry ... becoming a commercial scale developer and ...

When bacteria make large-scale changes to their chromosome structure, this is likely to have a dramatic impact on global gene expression levels, and indeed this was recently shown by members of the ...

eLife is a non-profit organisation inspired by research funders and led by scientists. Our mission is to help scientists accelerate discovery by operating a platform for research communication that ...