Pharma/biotech giants Pfizer PFE and Bristol Myers BMY boast of a dominant position in the lucrative oncology space. Oncology ...

NTRK-rearranged spindle cell neoplasms (NTRK-RSCNs) are an emerging soft tissue tumor entity characterized by NTRK gene fusions, occurring predominantly in the extremities of children and young adults ...

All NTRK gene fusions were identified by next-generation sequencing. Seven (23%) patients remained on treatment at the time of the data cutoff, 5 of whom had disease control. “These results ...

“We estimate that over 100 rare disease gene therapy products that had reached clinical stage have been discontinued since 2023 — not because of treatment failure, but because of the risk of market ...

Nine-month-old KJ Muldoon is the first patient to successfully receive personalized CRISPR gene editing therapy. After 300 days in the hospital, baby KJ has returned home.

So most fusion power concepts rely on “enriched” lithium, where the lithium-6 content has been boosted to more than 50 per cent, and sometimes up to 90 per cent, of the total.

Researchers at the University of California San Diego School of Medicine have developed a gene therapy for Alzheimer's disease that could help protect the brain from damage and preserve cognitive ...

The gene therapy technology was licensed by UC San Diego to Eikonoklastes Therapeutics in 2021. Eikonoklastes was granted Orphan Drug Designation (ODD) by the FDA for the use of the patented gene ...

The global fusion supply chain is expanding rapidly to support the “business of fusion”, according to the latest report by the Fusion Industry Association (FIA), The Fusion Industry Supply Chain – ...

An expert shares clinical pearls with the community, offering insights and tips for managing patients effectively. EP: 1.A 55-Year-Old Man with EGFR-mutated Advanced/Metastatic NSCLC EP: 2.Recent ...

The FDA granted Sarepta Therapeutics its first publicly documented Platform Technology Designation for a viral vector, called rAAVrh74, that the company uses in its investigational gene therapies..